With over 40% of all medicines in the pipeline aimed at rare diseases, the future looks positive for increasing the number of treatments available. However, as Ben Hargreaves discovers ...

Rare diseases aren’t as rare as the appellation suggests. For instance, according to the US Government Accountability Office, 30 million Americans have a rare disease, a little less than 10% of ...

Several companies, including ReGenTree, MimeTech, Oculis, and others are actively advancing treatments in the Neurotrophic Keratopathy market. < ...

Today, the Governments of Canada and the province of Saskatchewan signed the National Strategy for Drugs for Rare Disease (DRD) agreement to invest over $40 million over three years to improve access ...

Crinetics Pharmaceuticals is set for a fall 2025 launch of paltusotine, with strong Wall Street support despite being ...

This article is the product of a POLITICO Working Group presented by Sanofi and UCB. Of all the obstacles standing in the way of optimal care for rare disease patients and their families, doctors are ...

Recordati Industria Chimica e Farmaceutica SPAAz. Post raggruppamento Stock Snapshot Recordati Industria Chimica e Farmaceutica SPAAz. Post raggruppamento News More News Historical Prices for ...

Rare Diseases International, whose community engages with the World Health Organization, examines rare diseases and health equity, emphasising shifting the paradigm through global action Rare diseases ...